Precision BioSciences Gets Rare Pediatric Disease Status For Duchenne Muscular Dystrophy Therapy
25/6 13:40
(RTTNews) - Precision BioSciences, Inc. (DTIL) Wednesday said that the U.S. Food and Drug Administration (FDA) has granted Rare Pediatric Disease Designation for its gene therapy candidate PBGENE-DMD for the treatment of Duchenne muscular dystrophy (DMD), a genetic disorder chara...